Category Archives: cystic fibrosis
CF Rx: Exercise
Posted by cystic fibrosis, featured, medically unexplained symptoms
inWhen a Bad Animal Model is Good: Cystic Fibrosis
Posted by animal models, ATP12A, CFTR, cystic fibrosis, featured, Jackson lab, Kalydeco, medically unexplained symptoms, science
inNew Miracle Drugs: What Would You Pay?
Levi Collazo, a biology major at Southwestern Oklahoma State University, has cystic fibrosis (CF). “In the first photo, I was making fun of my own weight. I’ve always used humor as a defense mechanism. I weighed 110 pounds. I’m 5’10″. … Continue reading
The post New Miracle Drugs: What Would You Pay? appeared first on PLOS Blogs Network.
When Mutation Counters Infection: From Sickle Cell to Ebola
While pharmaceutical companies focus on drug discovery for Ebola virus disease, a powerful clue is coming from a rare “Jewish genetic disease” that destroys the brain. People with Niemann-Pick C1 disease can’t get Ebola, adding to the list of disease … Continue reading
The post When Mutation Counters Infection: From Sickle Cell to Ebola appeared first on PLOS Blogs Network.
A Checklist for Gene Therapy From the UK Cystic Fibrosis Trial
Washington, D.C. I’m at the American Society of Gene and Cell Therapy annual meeting, one of my favorite conferences. The very first talk provided a great example of why it is taking gene therapy so long to reach the …
The post A Checklist for Gene Therapy From the UK Cystic Fibrosis Trial appeared first on PLOS Blogs Network.